The TREATMENT Initiative

At Boston Children’s Hospital, we’re redefining what’s possible for children with rare genetic diseases.

The Targeted Research and Exploration Advancing Trial Models, Editing, and Next-generation Therapies (TREATMENT) Program brings together families, clinicians, and researchers to accelerate rare disease discovery and care.

Led by Dr. Wendy Chung, Chief of Pediatrics, the program combines Boston Children’s unmatched expertise in genetics, genomics, and translational medicine to bridge the gap between discovery and cure.

Our vision: a future where every child with a rare condition receives an early diagnosis, effective treatment, and lasting hope.

Stories of Hope and Discovery

At Boston Children’s Hospital, we’re redefining what’s possible for children with rare genetic diseases.

Stay up to date with the latest research breakthroughs, clinical trials, and family stories emerging from the TREATMENT Program.

Learn how scientists and families are working side-by-side to bring new treatments to life.